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Europe’s umbrella organization for 800 rare disease associations has developed a sweeping initiative to help the continent’s 30 million rare disease patients and their caregivers learn about their conditions, find assistance and receive treatment. Eurordis-Rare Diseases Europe hopes to improve the current piecemeal treatment and support program with a holistic,…

People with rare diseases know that the right government policies can make a big difference in the quality of their own lives, and those of their caregivers. But most lawmakers aren’t experts in even one well-known disease — let alone the world’s estimated 7,000 rare disorders. So how does the…

Myasthenia gravis (MG) patients who undergo thymectomy — surgery to remove the thymus gland — have a reduced risk of pulmonary infection and a shorter stay in intensive care when taken off mechanical ventilation support, called extubation, within six hours after surgery, a study suggests. The study, “Early extubation…

People with myasthenia gravis can develop psychiatric symptoms, including depression and insomnia. However, recommendations regarding safe medication are insufficient. In this case study, clinicians suggest that alpha-blockers are a potential safe therapeutic option for relieving insomnia and anxiety in a female myasthenia gravis patient. The case report, “Management of…

RaDaR, the catchy new name for the U.S. government-run Rare Diseases Registry Program, aims to help patient advocacy groups with limited resources build their own disease registries. The site was developed by the National Center for Advancing Translational Sciences (NCATS), a division of the National Institutes of…

Treatment with Rituxan (rituximab) led to high rates of clinical remission without posing significant side effects in a group of patients with myasthenia gravis (MG), a study shows. The study, “High efficacy of rituximab for myasthenia gravis: a comprehensive nationwide study in Austria,” was published in the…