News

Assessing altered eye movements with a technique called electrooculography (EOG) may become a non-invasive method for early diagnosis of myasthenia gravis (MG), according to new research. The study, “Analysis of Electrooculography Signals for the Detection of Myasthenia Gravis,” was published in the journal Clinical Neurophysiology.

The U.S. Food and Drug Administration (FDA) has granted orphan drug designation to zilucoplan, Ra Pharmaceuticals‘ lead candidate for the treatment of myasthenia gravis (MG). This status helps to support the potential therapy’s development by granting Ra Pharma certain incentives. Zilucoplan, formerly known as RA101495, is an…

Scientists discovered that patients with myasthenia gravis have a unique metabolic profile that can be used to diagnose the disorder, but also to predict the course of the disease and possibly lead to personalized treatments. The study, “Beyond the antibodies: serum metabolomic profiling of myasthenia gravis,” recently was…

Rare diseases deeply affect not only the children who experience them, but also their healthy brothers and sisters, as their parents can attest.    Two entries in November’s “Disorder: The Rare Disease Film Festival” will focus on what siblings go through, according to the San Francisco festival’s co-founder,…

Developing gene therapies for rare diseases is one thing. Creating gene-edited “designer babies” is quite another. German legal expert Timo Minssen outlined the potentially explosive ethical landmines surrounding such issues during a recent talk at the New York Genome Center. Minssen directs the Center for Advanced Studies in…

People with myasthenia gravis suffer from diverse patterns of muscle weakness, which tend to shift frequently throughout the disease’s course, a new study shows. The study, “Heterogeneity and Shifts in Distribution of Muscle Weakness in Myasthenia Gravis,” was published in the journal Neuromuscular Disorders. Myasthenia gravis (MG) is…