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November 13, 2018November 13, 2018

MicroRNA May Be New Therapeutic Target for Myasthenia Gravis, Mouse Study Shows

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A microRNA called miR-143, which blocks a molecule involved in the development and severity of myasthenia gravis, may be a new therapeutic target, according to a mouse study. The study, “MicroRNA-143 ... Read more

November 8, 2018November 8, 2018

Variations in Dendritic Cell Subtypes Could Predict Treatment Response in MG Patients, Study Suggests

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Changes in the ratio of dendritic cells (DCs), a subtype of immune cells, may reflect immune system function and could help predict treatment effectiveness in patients with myasthenia gravis ... Read more

November 6, 2018November 6, 2018

Women with MG Report More Frequent Intolerable Adverse Events on Prednisone, Study Finds

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Intolerable adverse events related to the use of prednisone, typically used to treat myasthenia gravis (MG), were more frequently reported by women than men, a study finds. The study, ... Read more

October 30, 2018

#NORDSummit – Major Issues on Table for Rare Disease Patients in US as Midterm Elections Approach

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With the U.S. midterm elections now less than two weeks away, patient advocacy groups are solidly focused on a range of hot-button issues, from the Orphan Drug Tax Creditand ... Read more

October 30, 2018October 30, 2018

Long-term RMET Found to Improve Patients’ Respiratory Endurance, Overall Health

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Long-term respiratory muscle endurance training (RMET) is a safe, feasible therapy that, in combination with conventional treatment, improves respiratory endurance and general well-being of people with mild to moderate ... Read more

October 25, 2018October 26, 2018

Presence of Anti-LRP4 Antibodies in Blood May Be Common to Myasthenia Gravis and ALS, Case Study Suggests

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Myasthenia gravis and amyotrophic lateral sclerosis (ALS) may share common underlying cellular mechanisms mediated by anti-LRP4 antibodies, a rare case report into both diseases being diagnosed in an elderly ... Read more

October 23, 2018October 23, 2018

Phase 2 Study Shows Rozanolixizumab Is Safe and Effective in Alleviating MG Symptoms

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Investigational antibody rozanolixizumab (UCB7665) has proven safe and effective in treating symptoms associated with myasthenia gravis (MG), Phase 2 results show. Based on the results of the MG0002 Phase ... Read more

October 18, 2018October 18, 2018

Gut Microbiota Differs in Myasthenia Gravis Patients, Pilot Study Reports

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Gut microbiota is altered in people with myasthenia gravis (MG), opening the door for exploring the use of microbiota-modulating therapies, like probiotics, as potential ways of better managing the disease. ... Read more

October 11, 2018October 11, 2018

Walk Tests a Reliable Measure of Exercise Capacity in MG Patients, Study Suggests

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Two timed walk tests were found to be highly reliable for the measurement of exercise capacity in patients with mild to moderate generalized myasthenia gravis (MG), a study reports. The ... Read more

October 9, 2018

Advocacy Groups, Doctors Question Rising Prices of Rare Disease Treatments

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Half a year has gone by since disgraced pharma executive Martin Shkreli was sentenced to seven years in federal prison for securities and wire fraud while heading San Diego-based ... Read more

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